Tag: Crispr

In the early 20th century, the discovery and mass production of penicillin transformed medicine, curing thousands of once-fatal bacterial infections and leading many to call it the first "miracle drug". But as pharmacology has evolved, the question of **what is the miracle drug?** has become less about a single cure and more about how medical innovation changes our lives.

In 2024, the FDA approved Casgevy, the first CRISPR-based gene therapy for sickle cell disease, demonstrating how a foundational scientific discovery can become a drug that opens the doors to a new drug, validating a new modality of medicine entirely. This landmark approval was the culmination of decades of research and has fundamentally shifted the paradigm for treating genetic disorders.

In a landmark decision in late 2023, the U.S. FDA approved Casgevy, the first treatment utilizing CRISPR technology to receive authorization. Understanding **how does casgevy gene therapy work** involves a look at its process of gene editing to enable a patient's body to produce healthy blood cells.