Skip to content

Tag: Hsc transplant

Explore our medication guides and pharmacology articles within this category.

Understanding How Does Libmeldy Work: A Gene Therapy for MLD

4 min read
Affecting approximately one in every 100,000 live births, metachromatic leukodystrophy (MLD) is a devastating genetic disorder. For eligible patients, the innovative one-time gene therapy, Libmeldy, offers a new approach to treatment, but understanding **how does libmeldy work** requires a deep dive into advanced molecular science.