What is apitegromab? An investigational muscle-targeted therapy for spinal muscular atrophy
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5 min read
According to developers at Scholar Rock, despite significant advances in treatments for spinal muscular atrophy (SMA), progressive muscle weakness remains a major unmet medical need. In this context, apitegromab is an investigational muscle-targeted therapy being developed to address the muscle atrophy and weakness that contribute to functional decline in SMA patients.