What is the current treatment for spinal muscular atrophy?
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5 min read
Spinal muscular atrophy (SMA) affects approximately 1 in 10,000 live births, making it the leading genetic cause of infant mortality [1.8.1, 1.8.2, 1.8.3]. So, what is the current treatment for spinal muscular atrophy that has transformed the outlook for this rare disease?
