What is the mechanism of action of Vyndaqel?
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4 min read
In transthyretin-mediated amyloidosis (ATTR), a progressive and often fatal disease, the transthyretin (TTR) protein misfolds and forms harmful amyloid deposits. The therapeutic effectiveness of Vyndaqel hinges on its unique ability to disrupt this process, making understanding what is the mechanism of action of Vyndaqel crucial for both patients and clinicians.
